An orphan disease is defined as a condition that affects fewer than 200,000 people nationwide. This includes diseases as familiar as cystic fibrosis, Lou Gehrig's disease, and Tourette's syndrome, and as unfamiliar as Hamburger disease, Job syndrome, and acromegaly, or "gigantism." Some diseases have patient populations of fewer than a hundred.
New rare diseases are discovered every year. Most are inherited and caused by alterations or defects in genes (mutations). Others can be acquired as a result of environmental and toxic conditions. Genes are pieces of DNA, part of the code that determines the traits and individual characteristics of all living things.

Market Analysis and Insights: Global Orphan Diseases Market
The global Orphan Diseases market size is projected to reach US$ 676.3 million by 2027, from US$ 260.3 million in 2020, at a CAGR of 14.1% during 2021-2027.
With industry-standard accuracy in analysis and high data integrity, the report makes a brilliant attempt to unveil key opportunities available in the global Orphan Diseases market to help players in achieving a strong market position. Buyers of the report can access verified and reliable market forecasts, including those for the overall size of the global Orphan Diseases market in terms of revenue.
On the whole, the report proves to be an effective tool that players can use to gain a competitive edge over their competitors and ensure lasting success in the global Orphan Diseases market. All of the findings, data, and information provided in the report are validated and revalidated with the help of trustworthy sources. The analysts who have authored the report took a unique and industry-best research and analysis approach for an in-depth study of the global Orphan Diseases market.

Global Orphan Diseases Scope and Market Size
Orphan Diseases market is segmented by company, region (country), by Type, and by Application. Players, stakeholders, and other participants in the global Orphan Diseases market will be able to gain the upper hand as they use the report as a powerful resource. The segmental analysis focuses on revenue and forecast by Therapy Area Type and by Application in terms of revenue and forecast for the period 2016-2027.

Segment by Therapy Area Type
Ocology
Hematology
Neurology
Endocrinology
Cardiovascular
Respiratory
Immunotherapy
Others

Segment by Application
Hospital Pharmacy
Retail Pharmacy
Others

By Region
North America
U.S.
Canada
Europe
Germany
France
U.K.
Italy
Russia
Nordic
Rest of Europe
Asia-Pacific
China
Japan
South Korea
Southeast Asia
India
Australia
Rest of Asia
Latin America
Mexico
Brazil
Rest of Latin America
Middle East & Africa
Turkey
Saudi Arabia
UAE
Rest of MEA

By Company
Bristol-Myers Squibb
Novartis
Celgene
Roche
Pfizer
Alexion
Sanofi
Vertex Pharmaceuticals
GlaxoSmithKline
Merck
Abbvie